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BridgeBio Pharma, Inc.

Pipeline5 assets

  • AcoramidisAttruby / TTR (Transthyretin) / Small Molecule / Genetic disease
    Early-Stage Variant Transthyretin Amyloidosis (ATTRv)Phase 3Under investigation
  • BBP-418BBP-418 / FKRP / Small Molecule / Genetic disease; neuromuscular
    Limb-Girdle Muscular Dystrophy Type 2I/R9 (LGMD2I/R9)Phase 3Investigational; FORTIFY interim analysis met endpoints
  • EncaleretCASR / Small Molecule / Endocrine; genetic disease
    Autosomal Dominant Hypocalcemia Type 1 (ADH1)Phase 3NDA planned/submission stated for H1 2026; pediatric registrational trial initiatedUSEUChronic HypoparathyroidismPhase 2NIH investigator-initiated study; Phase 3 planned in 2026
  • InfigratinibFGFR3 / Small Molecule / Skeletal dysplasia; genetic disease
    AchondroplasiaPhase 3PROPEL 3 registrational study; infant/toddler study enrollingUSEUHypochondroplasiaPhase 2ACCEL 2/3 Phase 2 portion dosed; data expected H2 2026
  • BBP-812BBP-812 / ASPA / Gene Therapy / Genetic disease; neurology
    Canavan DiseaseInvestigational AAV gene therapy

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BridgeBio Pharma, Inc. • Endpoint Arena