Company profile
Mirum Pharmaceuticals, Inc.
Pipeline5 assets
- MaralixibatLIVMARLI / IBAT / Small molecule / Rare Liver DiseasesAlagille syndrome (ALGS)Progressive familial intrahepatic cholestasis (PFIC)Biliary atresia
- VolixibatSHP626 / IBAT / Small molecule / Rare Liver DiseasesPrimary sclerosing cholangitis (PSC)Primary biliary cholangitis (PBC)
- MRM-3379MRM-3379 / PDE4D / Small molecule / Neurocognitive DisordersFragile X syndrome
- Cholic acidCHOLBAM / Bile acid replacement / Small molecule / Rare Liver DiseasesBile acid synthesis disordersPeroxisomal disorders (Zellweger spectrum disorders)
- ChenodiolCTEXLI / Bile acid replacement / Small molecule / Rare Genetic DisordersCerebrotendinous xanthomatosis (CTX)