Pipeline Watchlist

Company Pipelines

Recent additions

14 days
BCRX

Biocryst

Navenibart

STAR-0215 / Hereditary angioedema / Phase 3 / Hereditary angioedema prophylaxis

biocryst.com
AUTL

Autolus

obe-cel

obecabtagene autoleucel / Oncology; Autoimmune disease / Phase 1 / B-NHL

autolus.com
AURA

Aura Biosciences

belzupacap sarotalocan

AU-011 / oncology / Phase 3 / early choroidal melanoma (small choroidal melanoma and/or indeterminate lesions)

aurabiosciences.com
ATAI

Ataibeckley

Novel 5-HT2A Receptor Agonists

Mental health / In development / Opioid Use Disorder

ataibeckley.com
ASND

Ascendis Pharma

TransCon CNP + TransCon hGH

navapegritide + lonapegsomatropin / Endocrinology rare diseases / Phase 2 / Achondroplasia (children aged 2-11)

ascendispharma.com

Companies

ASND

Ascendis Pharma

5assets
  • TransCon hGHlonapegsomatropin / SKYTROFA / growth hormone receptor / long-acting TransCon prodrug of somatropin / Endocrinology rare diseases
    Turner syndrome (children aged 1-10)Phase 2New InsiGHTS TrialUnited StatesTurner syndrome, ISS, SHOX deficiency, SGA (children aged 2-17)Phase 3HighLiGHts TrialMultinationalPediatric GHDPhase 3Partner programChinaJapan
  • TransCon CNPnavapegritide / YUVIWEL / C-type natriuretic peptide pathway / long-acting TransCon prodrug of CNP / Endocrinology rare diseases
    Achondroplasia (infants aged 0-<2)Pivotal Phase 2reACHin TrialMultinationalAchondroplasia (children aged 2-11)Pivotal Phase 2ApproaCH TrialMultinationalAchondroplasia (adolescents aged 12-18)Pivotal Phase 2bteACH TrialMultinational
  • TransCon CNP + TransCon hGHnavapegritide + lonapegsomatropin / CNP pathway + growth hormone receptor / combination of long-acting TransCon prodrugs / Endocrinology rare diseases
    Achondroplasia (children aged 2-11)Phase 2COACH TrialMultinational
  • TransCon PTHpalopegteriparatide / YORVIPATH / parathyroid hormone receptor / long-acting TransCon prodrug of PTH / Endocrinology rare diseases
    Adult hypoparathyroidism (dosing expansion)Phase 3PaTHway60 TrialUnited StatesAdult hypoparathyroidismPhase 3Partner programChina
  • TransCon IL-2 β/γ (Systemic)IL-2 beta/gamma receptor / TransCon prodrug cytokine / Oncology
    Various tumor typesPhase 2IL-Believe TrialMultinational