Pipeline Watchlist

Company Pipelines

Recent additions

14 days
BCRX

Biocryst

Navenibart

STAR-0215 / Hereditary angioedema / Phase 3 / Hereditary angioedema prophylaxis

biocryst.com
AUTL

Autolus

obe-cel

obecabtagene autoleucel / Oncology; Autoimmune disease / Phase 1 / B-NHL

autolus.com
AURA

Aura Biosciences

belzupacap sarotalocan

AU-011 / oncology / Phase 3 / early choroidal melanoma (small choroidal melanoma and/or indeterminate lesions)

aurabiosciences.com
ATAI

Ataibeckley

Novel 5-HT2A Receptor Agonists

Mental health / In development / Opioid Use Disorder

ataibeckley.com
ASND

Ascendis Pharma

TransCon CNP + TransCon hGH

navapegritide + lonapegsomatropin / Endocrinology rare diseases / Phase 2 / Achondroplasia (children aged 2-11)

ascendispharma.com

Companies

AXSM
6assets
  • AXS-05AXS-05 / AUVELITY / NMDA receptor; sigma-1 receptor; CYP2D6 / oral small molecule / CNS
    Smoking cessationPhase 2/3 plannedon track to initiate in 2Q 2026US
  • SolriamfetolSUNOSI / dopamine and norepinephrine reuptake; TAAR1; 5-HT1A / oral small molecule / CNS
    Pediatric ADHDPhase 3 plannedtwo trials on track to initiate in 2Q 2026USMDD with excessive daytime sleepiness symptomsPhase 3CLARITY initiated February 2026USBinge eating disorderPhase 3ENGAGE ongoingUS
  • AXS-12AXS-12 / norepinephrine reuptake inhibitor; cortical dopamine modulator / oral small molecule / CNS
    Cataplexy in narcolepsyNDA submittedFDA filing acceptance decision pendingUS
  • AXS-14AXS-14 / norepinephrine reuptake inhibitor / oral small molecule / CNS
    FibromyalgiaPhase 3FORWARD ongoingUS
  • AXS-17AXS-17 / GABAA receptor alpha2,3 positive allosteric modulator / oral small molecule / CNS
    EpilepsyPhase 2-enablingtrial-enabling activities underwayUS
  • AXS-20AXS-20 / PDE10A / oral small molecule / CNS
    SchizophreniaPhase 3-enablingtrial-enabling activities anticipated in 2026USTourette syndromeplanned evaluationUS