Pipeline Watchlist

Company Pipelines

Recent additions

14 days
BCRX

Biocryst

Navenibart

STAR-0215 / Hereditary angioedema / Phase 3 / Hereditary angioedema prophylaxis

biocryst.com
AUTL

Autolus

obe-cel

obecabtagene autoleucel / Oncology; Autoimmune disease / Phase 1 / B-NHL

autolus.com
AURA

Aura Biosciences

belzupacap sarotalocan

AU-011 / oncology / Phase 3 / early choroidal melanoma (small choroidal melanoma and/or indeterminate lesions)

aurabiosciences.com
ATAI

Ataibeckley

Novel 5-HT2A Receptor Agonists

Mental health / In development / Opioid Use Disorder

ataibeckley.com
ASND

Ascendis Pharma

TransCon CNP + TransCon hGH

navapegritide + lonapegsomatropin / Endocrinology rare diseases / Phase 2 / Achondroplasia (children aged 2-11)

ascendispharma.com

Companies

BCRX

Biocryst

5assets
  • ORLADEYOberotralstat / ORLADEYO / plasma kallikrein / oral small-molecule inhibitor / Hereditary angioedema
    Hereditary angioedema prophylaxis, adults and pediatric patients 12 years and olderApproved/CommercialapprovedHereditary angioedema prophylaxis, pediatric patients 2 to <12 yearsApproved/Commercialapproved
  • NavenibartSTAR-0215 / plasma kallikrein / monoclonal antibody / Hereditary angioedema
    Hereditary angioedema prophylaxisPhase 3investigational
  • BCX17725BCX17725 / KLK5 / protein therapeutic / Rare disease
    Netherton syndromePhase 1investigational
  • Avoralstatplasma kallikrein / ocular plasma kallikrein inhibitor / Ophthalmology
    Diabetic macular edemainvestigational
  • STAR-0310STAR-0310 / OX40 / monoclonal antibody antagonist / Dermatology
    Atopic dermatitisinvestigational